PHAR 332

 

             

Biochemical Background

Genetics

Diagnostic Tests for MSUD

References

Clinical Cases

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Maple Syrup Urine Disease (MSUD) derives its name from the characteristic sweet smell, like that of maple syrup, of the urine of affected individuals. It is an autosomal recessive genetic disease, with an incidence of about 1 in 185,000 live births. The symptoms vary, some cases being more severe than others. The "classical" form of the disease appears within a few days after birth, when the smell of the infant's urine becomes noticeable. If untreated, MSUD can cause mental retardation; the severe form of the disease can involve convulsions, leading to coma and even death.